This study evaluated an investigational therapy for spinal muscular atrophy (SMA). To be eligible, participants had to be genetically diagnosed with SMA, presymptomatic and ≤ 6 weeks of age.
As time was of the essence, the sponsor wanted to implement a comprehensive travel and reimbursement program that would eliminate the logistical and financial concerns that could prevent a family from participating in the study.
The study leveraged BBK TravelTM as an adaptive solution that could fit the needs of all travelers.
Over the course of the study, there were several instances where the program evolved to meet the needs of this unique pediatric population. Some instances called for a patient ambassador to assist with translation, medical care and transportation. Other instances called for special overnight accommodations outside of a traditional hotel stay.
In reducing the time it might take sites to do this coordination, site staff were freed up to focus on patient care.
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