Familial Amyloid Polyneuropathy

PHASE 3

Key Takeaways

BBK Worldwide was engaged by a leading pharmaceutical company for more than six years to provide clinical study travel and reimbursement services for patients with familial amyloid polyneuropathy, a rare, inherited and progressive disease.

While our initial engagement focused on reimbursement, it expanded to include travel and then concluded with the introduction of medication delivery to support patients impacted by COVID-19 lockdown measures.

184 ENROLLED PATIENTS
24 SITES
9 COUNTRIES

Solution and Impact:
Medication Delivery

In the final year of BBK’s engagement, COVID-19 proved to be an unexpected challenge. It required a quick pivot to a solution that would support patients who needed to remain at home during lockdown. With speed and dexterity, we implemented our medication delivery service.

Medication was packaged at the site and then shipped directly to patients’ homes using ground and air methods. The shipments needed to be temperature-controlled between 2 and 8 degrees Celsius and ready for patients to self-administer upon delivery. The success of this program ensured that study participants were able to remain compliant with the protocol and that the sponsor was able to complete the study as planned.

4,561 Reimbursements

Reimbursement categories: meals, mileage, parking, lodging, ground transport, airfare, COVID-19 tests

6 COUNTRIES | 15 SITES

Argentina, Brazil, France, Spain, UK, US

863 Trips

1,606 itineraries translated into French, Portuguese and Spanish

4 COUNTRIES | 7 SITES

Argentina, Brazil, France, US

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Needham, MA 02494 United States

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Familial Amyloid Polyneuropathy

Key Takeaways

184 ENROLLED PATIENTS

24 SITES

9 COUNTRIES

The combination of services removed administrative burden for study staff while it created an optimal patient experience that succeeded in keeping patients engaged for the duration of the study.

Challenges

Solution and Impact:
Medication Delivery

2 SITES SUPPORTED IN BRAZIL

11 PATIENTS

18 MEDICATION DELIVERIES