Case Study — Pediatric Boys with Duchenne Muscular Dystrophy — Rare & Gene Therapy

Key Takeaways

This clinical study featured a novel investigational approach that appealed to physicians dedicated to advancing treatment options for pediatric patients with Duchenne muscular dystrophy (DMD) and their families.

Current treatment options were limited as they aimed to control symptoms and improve patient quality of life rather than cure the disease.

pediatric patients with Duchenne muscular dystrophy (DMD) and their families

Impact

Due to the rare nature of the condition and the small target audience, BBK developed a highly memorable study brand, creative messaging and engaging collateral that spoke to and motivated the parent caregiver audience to take action.

BBK’s materials were designed to keep the study top of mind at global study sites, as well as support patient identification and consent. The patient and referring-physician materials allowed site staff to quickly identify potentially eligible patients against key criteria while providing parent caregivers with the information necessary to foster consent.