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Duchenne Muscular Dystrophy


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Key Takeaways

This clinical study featured a novel investigational approach that appealed to physicians dedicated to advancing treatment options for pediatric patients with Duchenne muscular dystrophy (DMD) and their families.

Current treatment options were limited as they aimed to control symptoms and improve patient quality of life rather than cure the disease.

pediatric patients with Duchenne muscular dystrophy (DMD) and their families
DMD Messaging - Playing to Our Strengths


Despite being a rare pediatric disease, there was already a crowded clinical trial marketplace for DMD.

Only 13% of the DMD population have the specific gene mutation required to participate in the study.

The study was seeking a high number of patients over a long enrollment period.



The study logo was created to speak to the sponsor’s leadership position in the Duchenne space and to reflect the potential of the investigational drug to help prolong patient quality of life. The logo features exon 51 skipping to help referring physicians clearly identify the specific gene mutation associated with the study.


  • Proactively addresses study barriers and motivates parents and site staff with site-based educational
    study materials


  • Raises awareness among key opinion leaders and physician specialists to generate patient referrals



BBK’s in-house production and finishing helped to facilitate printed materials from design through approval and distribution.


Due to the rare nature of the condition and the small target audience, BBK developed a highly memorable study brand, creative messaging and engaging collateral that spoke to and motivated the parent caregiver audience to take action.

BBK’s materials were designed to keep the study top of mind at global study sites, as well as support patient identification and consent. The patient and referring-physician materials allowed site staff to quickly identify potentially eligible patients against key criteria while providing parent caregivers with the information necessary to foster consent.

DMD Creative Materials Collection
  • Increase-Referrals_ICON-1 153 PREQUALIFIED REFERRALS

  • Participants_ICON 152 ENROLLED PATIENTS


  • 7 SITES



Recruitment and Engagement Materials










MIS51ON Visit Guide and Bookmark


Visit-by-Visit Assessments Guide

A “punch card” bookmark was developed to track study visits and identify upcoming visits and associated assessments.



Appreciation Items

Appreciation items took into account the entire family. Parents were provided with a branded organizational folder for the family to keep all study-related documents.

Participating boys were given a study-branded backpack to
bring with them to their study visits.

Items were modest in cost and study-specific in nature, and they were readily approved by ethics committees.



MIS51ON Appreciation Items


Investigator Meeting Attendance


Investigator Meeting

BBK enlivened the Investigator Meeting with hero masks and study-branded T-shirts.



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